文献检索/Pharmacoepidemiology and Drug SafetyEM-T3Pharmacoepidemiology and Drug Safety2020-01-30第 29 卷第 10 期，1213-1218高影响力 · 前 1%Use of real‐world evidence in regulatory decisions for rare diseases in the United States—Current status and future directionsJasmanda WuSanofi (United States)Cunlin WangAscentage Pharma Group Inc. (United States)Sengwee TohHarvard UniversityFederica Edith PisaUCB Pharma (Belgium)Larry Bauer去出版社页面 引用论文图谱收藏 被引提醒分享打印登录后看摘要和中文要点英文摘要、AI 生成的中文摘要和三条要点、参考文献和引证文献列表、论文图谱，注册免费。登录 / 注册关键词real-world evidencerare diseasesorphan drugsFDA regulatory decision-makingreal-world datadisease registriesnatural history researchselection biasconfoundingpatient experience datacerliponase alfaasfotase alfauridine triacetaterare disease drug development参考文献2引证文献0相似文献引文网络关联作者相关机构登录后可以看完整列表。去登录论文图谱本篇和它的参考文献、引证文献、相似文献登录后可以看这篇的论文图谱：谁被它引用、谁引用了它、还有哪些相似的研究。登录 / 注册
