文献检索/Therapeutics and Clinical Risk ManagementEM-T3Therapeutics and Clinical Risk Management2024-09-01第 Volume 20 卷,641-652开放获取Experts’ Opinion in Fabry Disease Management and the Unmet Medical Need: The Saudi PerspectiveMajid AlfadhelKing Saud bin Abdulaziz University for Health SciencesNouriya Abbas Al-SannaaSaudi Aramco Medical Services OrganizationRawda SunbulQatif Central HospitalHuda Al-KhawajaSumayah AskandaraniKing Fahad Specialist HospitalTalal S.A. AlanziMamoun ElawadRiyadh Armed Forces HospitalCostas Fourtounas开放获取全文去出版社页面 引用论文图谱收藏 被引提醒分享打印登录后看摘要和中文要点英文摘要、AI 生成的中文摘要和三条要点、参考文献和引证文献列表、论文图谱,注册免费。登录 / 注册关键词Fabry diseasealpha-galactosidase Aenzyme replacement therapyunmet medical needslysosomal storage diseaseFASTEXearly diagnosisgenetic screeningbiomarkershome infusionpatient awarenessstigmauntreated patientsSaudi ArabiaGulf Cooperation Council参考文献26引证文献0相似文献引文网络关联作者相关机构登录后可以看完整列表。去登录论文图谱本篇和它的参考文献、引证文献、相似文献登录后可以看这篇的论文图谱:谁被它引用、谁引用了它、还有哪些相似的研究。登录 / 注册